4
Orphan Designations
0 approved, 4 designated
0
FDA Approvals
0
Active Trials
9
Rare Diseases
across 17 areas
0
News (30d)
Quiet
Oncovir is a company with 4 orphan drug designations across 9 rare diseases. 1 active policy bill affects their portfolio.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| Angelman syndrome | polyinosinic-polycytidilic acid | Des.TrialAppr. |
| acute sensory ataxic neuropathy | polyinosinic-polycytidilic acid | Des.TrialAppr. |
| aortic valve stenosis | polyinosinic-polycytidilic acid | Des.TrialAppr. |
| brain cancer | Poly-ICLC | Des.TrialAppr. |
| brainstem cancer | Poly-ICLC | Des.TrialAppr. |
| malignant carotid body paraganglioma | polyinosinic-polycytidilic acid (Poly-ICLC) | Des.TrialAppr. |
| post-treatment Lyme disease syndrome | polyinosinic-polycytidilic acid (Poly-ICLC) | Des.TrialAppr. |
| primary brain neoplasm | Poly-ICLC | Des.TrialAppr. |
| treatment-refractory schizophrenia | polyinosinic-polycytidilic acid (Poly-ICLC) | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
102
overlap in 2+ diseases
0/9
candidate diseases
0
avg importance: 0
1
affecting portfolio
0% of portfolio targets high unmet need diseases
102
overlap in 2+ diseases
0/9
candidate diseases
0
avg importance: 0
1
affecting portfolio