4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
39 companies found
70 approved / 109 designated
47 approved / 88 designated
41 designated · 0 approved
28 designated · 0 approved
9 approved / 24 designated
19 approved / 23 designated
9 approved / 23 designated
2 approved / 23 designated
11 designated · 0 approved
8 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved