4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
31 companies found
70 approved / 109 designated
47 approved / 88 designated
34 approved / 57 designated
43 designated · 0 approved
29 approved / 42 designated
41 designated · 0 approved
34 designated · 0 approved
14 approved / 34 designated
2 approved / 23 designated
13 designated · 0 approved
15 approved / 11 designated
10 designated · 0 approved
1 approved / 10 designated
6 approved / 6 designated
1 approved / 6 designated
5 designated · 0 approved
8 approved / 5 designated
5 designated · 0 approved
4 designated · 0 approved
1 approved / 4 designated
3 designated · 0 approved