4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
70 companies found
70 approved / 109 designated
47 approved / 88 designated
23 approved / 67 designated
34 approved / 57 designated
43 designated · 0 approved
10 approved / 43 designated
29 approved / 42 designated
41 designated · 0 approved
34 designated · 0 approved
14 approved / 34 designated
2 approved / 23 designated
5 approved / 14 designated
14 designated · 0 approved
11 approved / 14 designated
13 designated · 0 approved
17 approved / 13 designated
5 approved / 11 designated
15 approved / 11 designated
2 approved / 10 designated
1 approved / 10 designated
10 designated · 0 approved