4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
30 companies found
70 approved / 109 designated
43 designated · 0 approved
38 approved / 34 designated
34 designated · 0 approved
6 approved / 29 designated
1 approved / 25 designated
8 approved / 25 designated
3 approved / 20 designated
18 designated · 0 approved
15 designated · 0 approved
43 approved / 14 designated
6 approved / 11 designated
26 approved / 11 designated
10 designated · 0 approved
8 designated · 0 approved
4 approved / 6 designated
4 designated · 0 approved
1 approved / 4 designated
1 approved / 4 designated
4 designated · 0 approved
3 designated · 0 approved