4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
61 companies found
47 approved / 88 designated
23 approved / 67 designated
34 approved / 57 designated
43 designated · 0 approved
10 approved / 43 designated
29 approved / 42 designated
34 designated · 0 approved
14 approved / 34 designated
1 approved / 25 designated
19 designated · 0 approved
17 designated · 0 approved
2 approved / 13 designated
10 designated · 0 approved
4 approved / 10 designated
7 designated · 0 approved
7 designated · 0 approved
1 approved / 6 designated
5 designated · 0 approved
5 designated · 0 approved
1 approved / 5 designated
3 approved / 5 designated