4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
10 companies found
23 approved / 67 designated
10 approved / 43 designated
39 designated · 0 approved
19 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
1 approved / 2 designated
1 designated · 0 approved
1 designated · 0 approved