4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
46 companies found
70 approved / 109 designated
47 approved / 88 designated
23 approved / 67 designated
34 approved / 57 designated
10 approved / 43 designated
29 approved / 42 designated
39 designated · 0 approved
14 approved / 34 designated
26 approved / 30 designated
6 approved / 29 designated
22 designated · 0 approved
3 approved / 20 designated
17 designated · 0 approved
3 approved / 15 designated
15 designated · 0 approved
43 approved / 14 designated
13 designated · 0 approved
12 designated · 0 approved
1 approved / 11 designated
1 approved / 11 designated
11 designated · 0 approved