4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
155 companies found
70 approved / 109 designated
23 approved / 67 designated
39 designated · 0 approved
8 approved / 27 designated
9 approved / 23 designated
2 approved / 23 designated
38 approved / 22 designated
31 approved / 16 designated
15 designated · 0 approved
15 designated · 0 approved
2 approved / 13 designated
7 designated · 0 approved
7 designated · 0 approved
6 designated · 0 approved
1 approved / 6 designated
6 designated · 0 approved
2 approved / 5 designated
1 approved / 5 designated
5 designated · 0 approved
5 designated · 0 approved
1 approved / 5 designated