4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
7 companies found
23 designated · 0 approved
9 approved / 23 designated
19 designated · 0 approved
7 approved / 11 designated
5 designated · 0 approved
2 designated · 0 approved
1 approved / 1 designated