4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
26 companies found
43 designated · 0 approved
10 approved / 43 designated
29 approved / 42 designated
14 approved / 34 designated
9 approved / 24 designated
9 approved / 23 designated
23 designated · 0 approved
19 designated · 0 approved
10 designated · 0 approved
7 designated · 0 approved
7 designated · 0 approved
6 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved