4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
26 companies found
70 approved / 109 designated
47 approved / 88 designated
8 approved / 26 designated
23 designated · 0 approved
31 approved / 16 designated
6 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
15 approved / 1 designated
1 designated · 0 approved