4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
54 companies found
47 approved / 88 designated
23 approved / 67 designated
10 approved / 43 designated
14 approved / 34 designated
38 approved / 34 designated
26 approved / 30 designated
32 approved / 30 designated
1 approved / 25 designated
11 approved / 14 designated
5 approved / 11 designated
6 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved