4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
55 companies found
70 approved / 109 designated
47 approved / 88 designated
23 approved / 67 designated
34 approved / 57 designated
43 designated · 0 approved
34 designated · 0 approved
38 approved / 34 designated
6 approved / 29 designated
1 approved / 25 designated
8 approved / 25 designated
19 approved / 23 designated
38 approved / 22 designated
3 approved / 20 designated
18 designated · 0 approved
15 designated · 0 approved
43 approved / 14 designated
26 approved / 11 designated
6 approved / 11 designated
10 designated · 0 approved
10 designated · 0 approved
3 approved / 9 designated