4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
7 companies found
70 approved / 109 designated
3 approved / 15 designated
7 designated · 0 approved
5 designated · 0 approved
2 designated · 0 approved
9 approved / 1 designated
1 designated · 0 approved