4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
44 companies found
70 approved / 109 designated
10 approved / 43 designated
43 designated · 0 approved
41 designated · 0 approved
39 designated · 0 approved
34 designated · 0 approved
6 approved / 29 designated
8 approved / 27 designated
8 approved / 26 designated
17 designated · 0 approved
10 designated · 0 approved
7 designated · 0 approved
6 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved
1 approved / 4 designated
4 designated · 0 approved
3 designated · 0 approved
2 approved / 3 designated