4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
66 companies found
70 approved / 109 designated
47 approved / 88 designated
34 designated · 0 approved
38 approved / 34 designated
8 approved / 25 designated
15 designated · 0 approved
6 approved / 11 designated
7 designated · 0 approved
4 approved / 6 designated
4 approved / 6 designated
6 designated · 0 approved
1 approved / 5 designated
5 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
7 approved / 4 designated
3 designated · 0 approved
3 designated · 0 approved