4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
143 companies found
70 approved / 109 designated
47 approved / 88 designated
23 approved / 67 designated
34 approved / 57 designated
43 designated · 0 approved
10 approved / 43 designated
34 designated · 0 approved
32 approved / 30 designated
8 approved / 26 designated
9 approved / 24 designated
38 approved / 22 designated
19 designated · 0 approved
18 designated · 0 approved
17 designated · 0 approved
31 approved / 16 designated
43 approved / 14 designated
5 approved / 11 designated
1 approved / 11 designated
10 designated · 0 approved
9 designated · 0 approved
8 designated · 0 approved