4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
12 companies found
34 designated · 0 approved
9 approved / 23 designated
22 designated · 0 approved
1 approved / 10 designated
8 designated · 0 approved
7 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved