4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
96 companies found
47 approved / 88 designated
23 approved / 67 designated
43 designated · 0 approved
38 approved / 34 designated
14 approved / 34 designated
26 approved / 30 designated
1 approved / 25 designated
2 approved / 23 designated
11 approved / 15 designated
43 approved / 14 designated
11 designated · 0 approved
8 designated · 0 approved
2 approved / 7 designated
6 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved