4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
28 companies found
70 approved / 109 designated
47 approved / 88 designated
10 approved / 43 designated
43 designated · 0 approved
38 approved / 34 designated
26 approved / 30 designated
11 approved / 14 designated
13 designated · 0 approved
4 approved / 10 designated
7 designated · 0 approved
3 approved / 5 designated
4 designated · 0 approved
20 approved / 3 designated
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
4 approved / 2 designated
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved