4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
24 companies found
70 approved / 109 designated
47 approved / 88 designated
43 designated · 0 approved
34 designated · 0 approved
14 approved / 34 designated
32 approved / 30 designated
5 approved / 28 designated
8 approved / 27 designated
31 approved / 16 designated
3 approved / 15 designated
3 approved / 9 designated
1 approved / 8 designated
6 designated · 0 approved
6 designated · 0 approved
2 approved / 5 designated
4 designated · 0 approved
1 approved / 2 designated
3 approved / 2 designated
1 approved / 1 designated
1 designated · 0 approved
8 approved / 1 designated