4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
128 companies found
70 approved / 109 designated
47 approved / 88 designated
23 approved / 67 designated
34 approved / 57 designated
10 approved / 43 designated
43 designated · 0 approved
41 designated · 0 approved
39 designated · 0 approved
34 designated · 0 approved
32 approved / 30 designated
8 approved / 27 designated
38 approved / 22 designated
22 designated · 0 approved
3 approved / 20 designated
19 designated · 0 approved
15 designated · 0 approved
3 approved / 15 designated
43 approved / 14 designated
13 designated · 0 approved
12 designated · 0 approved
1 approved / 11 designated