4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
7 companies found
8 approved / 25 designated
2 approved / 23 designated
7 designated · 0 approved
4 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved