4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
13 companies found
34 approved / 57 designated
39 designated · 0 approved
26 approved / 30 designated
9 approved / 23 designated
15 designated · 0 approved
10 designated · 0 approved
5 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved