4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
6 companies found
9 designated · 0 approved
5 designated · 0 approved
3 approved / 5 designated
6 approved / 4 designated
3 designated · 0 approved
1 designated · 0 approved