4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
28 companies found
23 approved / 67 designated
34 designated · 0 approved
38 approved / 22 designated
15 designated · 0 approved
43 approved / 14 designated
9 designated · 0 approved
10 approved / 9 designated
7 designated · 0 approved
6 designated · 0 approved
1 approved / 5 designated
4 designated · 0 approved
4 designated · 0 approved
5 approved / 4 designated
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved