4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
7 companies found
14 approved / 34 designated
1 approved / 25 designated
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved