4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
6 companies found
39 designated · 0 approved
38 approved / 34 designated
1 approved / 25 designated
4 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved