4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
59 companies found
70 approved / 109 designated
47 approved / 88 designated
23 approved / 67 designated
10 approved / 43 designated
43 designated · 0 approved
29 approved / 42 designated
41 designated · 0 approved
39 designated · 0 approved
14 approved / 34 designated
38 approved / 34 designated
26 approved / 30 designated
6 approved / 29 designated
5 approved / 28 designated
8 approved / 26 designated
8 approved / 25 designated
38 approved / 22 designated
31 approved / 16 designated
15 designated · 0 approved
3 approved / 15 designated
13 designated · 0 approved
11 designated · 0 approved