4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
14 companies found
47 approved / 88 designated
39 designated · 0 approved
9 approved / 7 designated
1 approved / 6 designated
5 designated · 0 approved
4 designated · 0 approved
2 approved / 3 designated
8 approved / 3 designated
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved