4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
61 companies found
47 approved / 88 designated
23 approved / 67 designated
14 approved / 34 designated
26 approved / 30 designated
9 approved / 23 designated
49 approved / 9 designated
1 approved / 8 designated
9 approved / 7 designated
6 designated · 0 approved
1 approved / 6 designated
5 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
4 approved / 3 designated
3 designated · 0 approved
4 approved / 3 designated
3 designated · 0 approved
3 designated · 0 approved