4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
54 companies found
70 approved / 109 designated
23 approved / 67 designated
43 designated · 0 approved
41 designated · 0 approved
14 approved / 34 designated
6 approved / 29 designated
1 approved / 25 designated
43 approved / 14 designated
10 designated · 0 approved
7 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
1 approved / 4 designated
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved