4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
23 companies found
34 approved / 57 designated
29 approved / 42 designated
6 approved / 29 designated
23 designated · 0 approved
3 approved / 15 designated
13 designated · 0 approved
26 approved / 11 designated
6 designated · 0 approved
3 approved / 5 designated
6 approved / 4 designated
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 approved / 1 designated
1 designated · 0 approved
1 designated · 0 approved