4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
10 companies found
47 approved / 88 designated
5 approved / 28 designated
1 approved / 25 designated
9 approved / 23 designated
13 designated · 0 approved
11 designated · 0 approved
3 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved
1 designated · 0 approved