4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
14 companies found
9 approved / 24 designated
19 designated · 0 approved
16 designated · 0 approved
81 approved / 8 designated
5 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
1 approved / 3 designated
2 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved