4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
8 companies found
4 approved / 3 designated
32 approved / 3 designated
1 designated · 0 approved
33 approved / 1 designated
1 designated · 0 approved
1 designated · 0 approved
4 approved / 1 designated
1 designated · 0 approved