4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
15 companies found
47 approved / 88 designated
8 approved / 26 designated
10 designated · 0 approved
9 designated · 0 approved
4 designated · 0 approved
1 approved / 4 designated
2 approved / 3 designated
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved