4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
7 companies found
47 approved / 88 designated
41 designated · 0 approved
39 designated · 0 approved
2 approved / 3 designated
2 designated · 0 approved
4 approved / 2 designated
1 designated · 0 approved