4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
6 companies found
47 approved / 88 designated
9 approved / 24 designated
8 designated · 0 approved
5 approved / 2 designated
15 approved / 1 designated
1 designated · 0 approved