4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
193 companies found
70 approved / 109 designated
47 approved / 88 designated
23 approved / 67 designated
34 approved / 57 designated
43 designated · 0 approved
10 approved / 43 designated
29 approved / 42 designated
41 designated · 0 approved
39 designated · 0 approved
34 designated · 0 approved
14 approved / 34 designated
32 approved / 30 designated
26 approved / 30 designated
28 designated · 0 approved
8 approved / 26 designated
9 approved / 24 designated
2 approved / 23 designated
22 designated · 0 approved
3 approved / 20 designated
17 designated · 0 approved
15 designated · 0 approved