4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
35 companies found
34 approved / 57 designated
39 designated · 0 approved
34 designated · 0 approved
5 approved / 28 designated
8 approved / 26 designated
38 approved / 22 designated
31 approved / 16 designated
2 approved / 13 designated
8 designated · 0 approved
1 approved / 6 designated
4 approved / 6 designated
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved
2 designated · 0 approved
1 approved / 2 designated