4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
23 companies found
70 approved / 109 designated
6 approved / 11 designated
9 designated · 0 approved
1 approved / 6 designated
5 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
2 approved / 4 designated
3 designated · 0 approved
5 approved / 2 designated
2 designated · 0 approved
1 approved / 2 designated
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved