4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
39 companies found
23 approved / 67 designated
43 designated · 0 approved
5 approved / 28 designated
1 approved / 25 designated
23 designated · 0 approved
81 approved / 8 designated
8 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved