4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
7 companies found
70 approved / 109 designated
23 approved / 67 designated
43 designated · 0 approved
19 designated · 0 approved
15 designated · 0 approved
2 approved / 5 designated
5 designated · 0 approved