4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
9 companies found
47 approved / 88 designated
29 approved / 42 designated
1 approved / 25 designated
9 approved / 24 designated
10 designated · 0 approved
5 approved / 2 designated
1 designated · 0 approved
15 approved / 1 designated
1 designated · 0 approved