4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
118 companies found
70 approved / 109 designated
47 approved / 88 designated
29 approved / 42 designated
5 approved / 28 designated
8 approved / 26 designated
9 approved / 24 designated
15 designated · 0 approved
5 approved / 14 designated
9 designated · 0 approved
9 designated · 0 approved
7 designated · 0 approved
6 designated · 0 approved
6 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved