4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
6 companies found
10 approved / 9 designated
1 approved / 5 designated
2 designated · 0 approved
18 approved / 2 designated
1 designated · 0 approved
1 designated · 0 approved