Comprehensive, easy-to-understand information about this condition
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Kisho delivers this disease record via API, including phenotypes (HPO), genes, orphan drug designations, screening status, and PAG mapping, with version history and governance.
Organizations with orphan designations or approved therapies for this disease
Bioverativ Therapeutics, Inc.
Other
GC Biopharma Corp.
Other
Genentech, Inc.
Other
Genzyme Corporation
Other
Novo Nordisk
Other
Takeda Development Center Americas, Inc.
Other
Takeda Pharmaceuticals U.S.A., Inc.
Other
Wyeth Pharmaceuticals LLC, a subsidiary of Pfizer Inc.
Other