Disease that occurs as a consequence of immunosuppression in a recipient of a hematopoietic stem cell transplant, or as a consequence of the transplantation.
Comprehensive, easy-to-understand information about this condition
How we create this content →Patient Advocacy Groups (PAGs) provide support, resources, and community for patients and caregivers.
Consider asking your healthcare providers these condition-specific questions
Patient Advocacy Groups (PAGs) provide support, resources, and community for patients and caregivers.
Consider asking your healthcare providers these condition-specific questions
The documentation for this condition is limited primarily due to its rarity and the complexities of post-transplant complications. As this disease affects a small subset of individuals, systematic clinical studies have been scarce. Additionally, the overlapping symptoms with other transplant-related conditions complicate the characterization and understanding of this disease.
To navigate your care effectively, consider seeking a specialist in hematology or a transplant physician with expertise in post-transplant complications. The National Stem Cell Foundation (https://nationalstemcellfoundation.org) can provide valuable resources and support. Additionally, inquire about participation in clinical trials, as they may offer access to cutting-edge treatments and contribute to the understanding of this condition. Genetic counseling may also be beneficial, especially if there are concerns about familial implications.
There are currently 12 active clinical trials exploring various aspects of this condition. Notably, there are orphan drug designations for human monoclonal antibody inhibitors of mannan binding lectin-associated serine protease-2 (MASP-2) and Ravulizumab, which are in development. For more information on ongoing trials, you can visit the ClinicalTrials.gov search page: https://clinicaltrials.gov/search?cond=disease%20related%20to%20hematopoietic%20stem%20cell%20transplant.
Actionable guidance for navigating care for disease related to hematopoietic stem cell transplant
To navigate your care effectively, consider seeking a specialist in hematology or a transplant physician with expertise in post-transplant complications. The National Stem Cell Foundation (https://nationalstemcellfoundation.org) can provide valuable resources and support. Additionally, inquire about participation in clinical trials, as they may offer access to cutting-edge treatments and contribute to the understanding of this condition. Genetic counseling may also be beneficial, especially if there are concerns about familial implications.
Consider asking your healthcare providers these condition-specific questions
Connect with organizations supporting the disease related to hematopoietic stem cell transplant community
Helpful links for rare disease information and support
Clinical profile data for this condition is not yet available. Phenotype information may still be loading below.
Research studies investigating treatments and therapies for this condition.
Active Trials
Total Trials
Data from ClinicalTrials.gov Feb 8, 2026
Patient Advocacy Groups (PAGs) provide support, resources, and community for patients and caregivers.
Consider asking your healthcare providers these condition-specific questions
AI-Generated Content: This summary was generated using AI. Content has been fact-checked. Always consult with qualified healthcare providers for medical guidance.
Organizations with approved therapies for this disease
No approved therapies yet
Research is ongoing — 4 companies have orphan drug designations for this disease
Kisho delivers this disease record via API, including phenotypes (HPO), genes, orphan drug designations, screening status, and PAG mapping, with version history and governance.